Failure of a gene-reading quality-control mechanism called Integrator leaves cells littered with abnormal RNA strands that ...

If administered early, gene therapy has the potential to change the medical ... is able to preserve motor function and ...

"Moreover, the duration of follow-up is among the longest reported for a lentiviral vector-based gene therapy; 13 patients ...

Failure of a gene-reading quality-control mechanism called Integrator leaves cells littered with abnormal RNA strands that ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, ...

Actor Gene Hackman had not eaten for quite some time before his death, a final autopsy report has revealed, though heart disease was the ultimate cause. The Office of the Medical Investigator in ...

Gene therapy has emerged as a promising approach to previously untreatable conditions, including Duchenne muscular dystrophy (DMD), a progressive disorder caused by DMD mutations that leads to early ...

Additionally, it shows "leaky" pulsatile gene function when it is supposedly switched off. So, how did such a high-tech piece of engineering come to exist in a commonplace organism, and why does ...

SANTA FE, N.M. — The main cause of Gene Hackman's death was heart disease, but he was also in the advanced stages of Alzheimer's disease and likely had not eaten for a long time, according to a ...