The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...

A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

KJ Muldoon became the first patient to undergo personalized CRISPR treatment, a therapy that found the one uniquely mutated gene out of 20,000 in his little body, and fixed it.

A newborn boy, KJ, was diagnosed at birth with a rare and potentially fatal genetic disease. He received a novel, on-demand CRISPR therapy in record time.

Prader-Willi syndrome is a rare genetic disease that causes poor feeding in infancy but later triggers insatiable hunger.

Bilharzia – or schistosomiasis – is a human parasitic disease predominant in tropical areas. It is classified as one of 20 ...

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