Aplastic anaemia is a rare, life‐threatening disorder of the bone marrow characterised by pancytopenia and a hypocellular marrow. The primary pathophysiology involves immune-mediated destruction of ...
Eltrombopag combined with immunosuppressive therapy in pediatric patients with severe aplastic anemia achieved a 54.9% overall response rate at 26 weeks, with a 71.4% response in relapsed/refractory ...
The FDA has approved omidubicel-onlv (Omisirge, Gamida Cell Ltd.) as the first hematopoietic stem cell transplant therapy for patients with severe aplastic anemia (SAA). Specifically, omidubicel is ...