LYON, France--(BUSINESS WIRE)--Regulatory News: POXEL SA (Euronext: POXEL - FR0012432516), a clinical stage biopharmaceutical company developing innovative treatments for chronic serious diseases with ...

A gene therapy to treat cerebral adrenoleukodystrophy (CALD) -- a neurodegenerative disease that typically claims young boys' lives within 10 years of diagnosis -- effectively stabilized the disease's ...

LYON, France--(BUSINESS WIRE)--POXEL SA (Euronext: POXEL - FR0012432516), a clinical stage biopharmaceutical company developing innovative treatments for chronic serious diseases with metabolic ...

KUTV — The Utah Department of Health’s Newborn Screening (NBS) program has added a test for all babies born in the state that detects a debilitating genetic disorder. On Sept. 20, 2020, the NBS ...

Lenti-D hematopoietic stem cell gene therapy stabilizes neurologic function in boys with cerebral adrenoleukodystrophy (ALD-102 and ALD-104) Presenting Author: Dr. Jörn-Sven Kühl, Department of ...

Adrenoleukodystrophy (ALD) is rare X-linked genetic disease that affects the adrenal glands (found on top of the kidneys) as well as the myelin in the brain and spinal cord. The incidence of ALD is ...

90% of evaluable patients (27/30) alive and free of major functional disabilities (MFDs) at two years follow-up in Phase 2/3 Starbeam study (ALD-102) Patients in long-term follow-up study (LTF-304) ...

A strategy that combines gene therapy with blood stem cell therapy may be a useful tool for treating a fatal brain disease, French researchers have found. A strategy that combines gene therapy with ...

Considering taking supplements to treat Adrenoleukodystrophy ald? Below is a list of common natural remedies used to treat or reduce the symptoms of Adrenoleukodystrophy ald. Follow the links to read ...